With this approval, approximately 1,500 children will be eligible for a CFTR modulator for the first time. Today’s news is a significant step forward in our mission to help all people with CF lead long, fulfilling lives, as research suggests that beginning treatment with a modulator early could help slow or even prevent the irreversible progression of cystic fibrosis.
If you’re a parent or caregiver to a child with CF, join us for a community webinar from 7-8 p.m. ET on Thursday, June 10, to have your top questions answered by experts from the Cystic Fibrosis Foundation. All those who register will receive a recording of the event.
It is thanks to your participation in clinical trials and fundraising efforts that we have been able to reach this important milestone. Together, we will not stop until everyone has a treatment for the underlying cause of their disease.